Subjects
- Rare Diseases -- drug therapy[remove]3
- United States3
- United States. Food and Drug Administration2
- Biological Products1
- Drug Approval -- organization & administration1
- Drug Development1
- Drug Development -- organization & administration1
- Drug Development -- standards1
- Drug Industry1
- Drugs, Investigational1
- Government Regulation1
- Metabolism, Inborn Errors -- drug therapy1
- United States. Department of Health and Human Services1
