Subjects: Genetic Therapy - Digital Collections - National Library of Medicine Search Results

Start Over Subjects Genetic Therapy ✖

1. Letter from Bernard D. Davis to Maxine Singer

Publication:: Produced: 10 March 1992
Subject(s):: Scientific Misconduct
Genetic Therapy
Archival Collection:: The Maxine Singer Papers (Profiles in Science)

2. Voretigene neparvovec for biallelic RPE65-mediated retinal disease: effectiveness and value : final evidence report

Publication:: [Boston, Massachusetts] : Institute for Clinical and Economic Review, February 14, 2018
Subject(s):: Genetic Therapy
Leber Congenital Amaurosis -- genetics
Leber Congenital Amaurosis -- therapy
Retinal Diseases -- genetics
Retinal Diseases -- therapy
Retinal Pigment Epithelium -- abnormalities
Mutation
Randomized Controlled Trials as Topic
Treatment Outcome
Visual Acuity
Humans
United States

3. Chemistry, manufacturing, and control (CMC) information for human gene therapy investigational new drug applications (INDs)

Publication:: Silver Spring, MD : Center for Biologics Evaluation and Research, January 2020
Subject(s):: Chemistry, Pharmaceutical
Genetic Therapy
Investigational New Drug Application
Drugs, Investigational
Quality Control
United States
United States. Department of Health and Human Services.
United States. Food and Drug Administration.

4. Human gene therapy for retinal disorders

Publication:: Silver Spring, MD : Center for Biologics Evaluation and Research, January 2020
Subject(s):: Clinical Trials as Topic
Genetic Therapy
Drug Evaluation, Preclinical
Retinal Diseases -- therapy
Investigational New Drug Application
United States
United States. Department of Health and Human Services.
United States. Food and Drug Administration.

5. Testing of retroviral vector-based human gene therapy products for replication competent retrovirus during product manufacture and patient follow-up

Publication:: Silver Spring, MD : Center for Biologics Evaluation and Research, January 2020
Subject(s):: Drug Contamination
Genetic Therapy
Genetic Vectors
Retroviridae
Virus Replication
United States
United States. Department of Health and Human Services.
United States. Food and Drug Administration.

6. Human gene therapy for rare diseases

Publication:: Silver Spring, MD : Center for Biologics Evaluation and Research, January 2020
Subject(s):: Drug Development
Genetic Therapy
Rare Diseases -- therapy
Clinical Trials as Topic
Drug Evaluation, Preclinical
United States
United States. Department of Health and Human Services.
United States. Food and Drug Administration.

7. Human gene therapy for hemophilia

Publication:: Silver Spring, MD : Center for Biologics Evaluation and Research, January 2020
Subject(s):: Genetic Therapy
Hemophilia A -- drug therapy
Hemophilia B -- drug therapy
Clinical Trials as Topic
Drug Evaluation, Preclinical
Factor VIII -- therapeutic use
Factor IX -- therapeutic use
United States
United States. Department of Health and Human Services.
United States. Food and Drug Administration.

8. The National Institutes of Health presents a conference on human gene therapy: December 4-6, 1991, Masur Auditorium, National Institutes of Health, Bethesda, Maryland

Publication:: Bethesda, Md. : National Heart, Lung, and Blood Institute, 1991
Subject(s):: Genetic Therapy

9. Human gene therapy

Publication:: [Bethesda, Md. : Medical Arts and Photography Branch, National Institutes of Health, 1992]
Subject(s):: Genetic Therapy

10. Animal research will make gene therapy happen

Publication:: [Bethesda, Md.] : NIH Animal Research Advisory, [19--]
Subject(s):: Animal Experimentation
Animals, Laboratory
Genetic Therapy