NLM Digital Collections


Search Constraints

Start Over You searched for: Subjects Genetic Therapy Remove constraint Subjects: Genetic Therapy

Search Results

2. Voretigene neparvovec for biallelic RPE65-mediated retinal disease: effectiveness and value : final evidence report

3. Chemistry, manufacturing, and control (CMC) information for human gene therapy investigational new drug applications (INDs)

5. Testing of retroviral vector-based human gene therapy products for replication competent retrovirus during product manufacture and patient follow-up

7. Human gene therapy for hemophilia

9. Human gene therapy