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1. Gene therapy for hemophilia B and an update on gene therapy for hemophilia A: effectiveness and value : final evidence report

Author(s):

Tice, Jeffrey A., author
Chu, Janet N., author
Moradi, Ashton, author
Herce-Hagiwara, Belen, author
Fahim, Shahariar Mohammed, author
Agboola, Foluso, author
Pearson, Steven D., author
Rind, David M., author
Walton, Surrey M., author
Sarker, Jyotirmoy, author

Publication:

[Boston, Massachusetts] : Institute for Clinical and Economic Review, December 22, 2022

Subject(s):

Antibodies, Bispecific
Antibodies, Monoclonal, Humanized
Cost-Effectiveness Analysis
Genetic Therapy
Hemophilia A -- therapy
Hemophilia B -- therapy
United States

2. Valoctocogene roxaparvovec and emicizumab for hemophilia A without inhibitors: effectiveness and value : final report

Author(s):

Rind, David M., author
Walton, Surrey M., author
Agboola, Foluso, author
Herron-Smith, Serina, author
Quach, Danny, author
Chapman, Rick M., author
Pearson, Steven D., author
Bradt, Pamela, author

Publication:

[Boston, Massachusetts] : Institute for Clinical and Economic Review, November 20, 2020

Subject(s):

Antibodies, Monoclonal
Genetic Therapy
Hemophilia A -- drug therapy
United States

3. Mavacamten for hypertrophic cardiomyopathy: effectiveness and value : final evidence report and meeting summary

Author(s):

Wasfy, Jason H., author
Walton, Surrey M., author
Beinfeld, Molly, author
Nhan, Emily, author
Sarker, Jyotirmoy, author
Whittington, Melanie D., author
Pearson, Steven D., author
Rind, David M., author

Publication:

[Boston, Massachusetts] : Institute for Clinical and Economic Review, November 16, 2021

Subject(s):

Cardiac Myosins -- antagonists & inhibitors
Cardiomyopathy, Hypertrophic -- drug therapy
United States