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1. Gene therapies for sickle cell disease: final evidence report

Author(s):

Beaudoin, Francesca, author
Nikitin, Dmitriy, author
Campbell, Jonathan D., author
McKenna, Avery, author
Pearson, Steven D., author
Rind, David M., author
Thokala, P. (Praveen), author
Spackman, David Eldon, author

Publication:

[Boston, Massachusetts] : Institute for Clinical and Economic Review, August 21, 2023

Subject(s):

Anemia, Sickle Cell -- therapy
Genetic Therapy
United States

2. Belimumab and voclosporin for lupus nephritis: effectiveness and value : final report

Author(s):

Tice, Jeffrey A., author
Agboola, Foluso, author
Herron-Smith, Serina, author
Chapman, Rick, (Of Institute for Clinical and Economic Review), author
Pearson, Steven D., author
Mandrik, Olena, author
Thokala, P. (Praveen), author
Fotheringham, James, (Of University of Sheffield), author

Publication:

[Boston, Massachusetts] : Institute for Clinical and Economic Review, April 16, 2021

Subject(s):

Antibodies, Monoclonal, Humanized
B-Cell Activating Factor -- antagonists & inhibitors
Calcineurin Inhibitors -- therapeutic use
Cyclosporine -- therapeutic use
Immunosuppressive Agents -- therapeutic use
Lupus Nephritis -- drug therapy
Treatment Outcome
United States

3. Spinraza and Zolgensma for spinal muscular atrophy: effectiveness and value : final evidence report

Author(s):

Ellis, Alexandra, author
Mickle, Kristin, author
Herron-Smith, Serina, author
Kumar, Varun M., author
Cianciolo, Laura, author
Seidner, Matt, author
Rind, David, author
Pearson, Steven, author
Thokala, P. (Praveen), author
Stevenson, M. (Matt), author

Publication:

[Boston, Massachusetts] : Institute for Clinical and Economic Review, May 24, 2019

Subject(s):

Genetic Therapy
Muscular Atrophy, Spinal -- drug therapy
United States